Cat. No. | Product Name | Target | Signaling Pathways |
---|---|---|---|
T16757 |
Risdiplam
RO7034067,RG7916 |
DNA/RNA Synthesis | Cell Cycle/Checkpoint; DNA Damage/DNA Repair |
Risdiplam (RO7034067) 是一种中枢和外周分布的 SMN2 前 mRNA 剪接修饰剂,可增加运动神经元存活 (SMN) 蛋白水平。 |