Cat. No. | Product Name | Target | Signaling Pathways |
---|---|---|---|
T12718L |
RG7800
RO6885247 |
Others; DNA/RNA Synthesis | Cell Cycle/Checkpoint; DNA Damage/DNA Repair; Others |
RG7800 (RO6885247) 是一种 SMN2 拼接修饰剂,有用于治疗脊髓性肌萎缩的研究潜力。 | |||
T78046 |
RG7800 tetrahydrochloride
RO6885247 tetrahydrochloride |
DNA/RNA Synthesis | Cell Cycle/Checkpoint; DNA Damage/DNA Repair |
RG7800 hydrochloride为一可口服SMN2剪接调节剂,其对SMN2剪接及SMN蛋白的EC1.5x值分别为23 nM及87 nM。 | |||
T12718 |
RG7800 hydrochloride (1449598-06-4 free base)
RO6885247 hydrochloride,RG7800 hydrochloride |
Others | Others |
RG7800 hydrochloride is an orally active modulator of SMN2 splicing. | |||
T64288 | RG7800 hydrochloride | ||
RG7800 hydrochloride 是一种口服具有活力的 SMN2 剪接调节剂,能够作用于 SMN2 剪接 (EC1.5x: 23 nM) 及 SMN 蛋白 (EC1.5x: 87 nM)。 |