Cat. No. | Product Name | Target | Signaling Pathways |
---|---|---|---|
T12718L |
RG7800
RO6885247 |
Others; DNA/RNA Synthesis | Cell Cycle/Checkpoint; DNA Damage/DNA Repair; Others |
RG7800 (RO6885247) 是一种 SMN2 拼接修饰剂,有用于治疗脊髓性肌萎缩的研究潜力。 | |||
T12718 |
RG7800 hydrochloride (1449598-06-4 free base)
RO6885247 hydrochloride,RG7800 hydrochloride |
Others | Others |
RG7800 hydrochloride is an orally active modulator of SMN2 splicing. |