Cat. No. | Product Name | Target | Signaling Pathways |
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T38986 |
Fitusiran
ALN-AT3SC,SAR439774 |
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Fitusiran (ALN-AT3SC) is a small interfering RNA compound designed to selectively bind to antithrombin (AT) messenger RNA in the liver, leading to decreased AT production. By doing so, Fitusiran enhances thrombin generation, making it a promising candidate for hemophilia research. | |||
T74877 |
GalNAc unconjugated/naked Fitusiran
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GalNAc unconjugated/naked Fitusiran 是一种没有偶联 GalNAc 的小干扰 RNA,专门针对抗凝血酶(AT)信使 RNA,以降低肝脏中 AT 的产生。GalNAc unconjugated/naked Fitusiran 增加凝血酶的生成,并可用于血友病的研究。 |