Cat. No. | Product Name | Target | Signaling Pathways |
---|---|---|---|
T66481 |
TG-693
|
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TG693, an orally available inhibitor of CLK1, promotes the skipping of the endogenous mutated exon 31 in Duchenne muscular dystrophy (DMD) patient-derived cells and increased the production of the functional exon 31-skipped dystrophin protein. |